2025
Permutation tests for detecting treatment effect heterogeneity in cluster randomized trials
Maleyeff L, Li F, Haneuse S, Wang R. Permutation tests for detecting treatment effect heterogeneity in cluster randomized trials. Statistical Methods In Medical Research 2025, 34: 1617-1632. PMID: 40525570, PMCID: PMC12365356, DOI: 10.1177/09622802251348999.Peer-Reviewed Original ResearchCluster randomized trialDetect treatment effect heterogeneityTreatment effect heterogeneityEffect heterogeneityNominal type I error rateRandomized trialsType I error rateTreatment-covariate interactionsAssess treatment effect heterogeneityTests of interaction termsPermutation testAverage treatment effectPain programEvaluation of intervention strategiesParametric assumptionsEffect modificationHealthcare ResearchActive copingSimulation studyTreatment effectsIntervention strategiesTrial contextPermutationInteraction termsTrials
2024
Assessing treatment effect heterogeneity in the presence of missing effect modifier data in cluster-randomized trials
Blette B, Halpern S, Li F, Harhay M. Assessing treatment effect heterogeneity in the presence of missing effect modifier data in cluster-randomized trials. Statistical Methods In Medical Research 2024, 33: 909-927. PMID: 38567439, PMCID: PMC11041086, DOI: 10.1177/09622802241242323.Peer-Reviewed Original ResearchConceptsMultilevel multiple imputationHeterogeneous treatment effectsCluster randomized trialPotential effect modifiersMultiple imputationAssess treatment effect heterogeneityEffect modifiersTreatment effect heterogeneityComplete-case analysisMissingness mechanismIntracluster correlationSimulation studyUnder-coverageRandomized trialsEffect heterogeneityHealth StudyTreatment effectsContinuous outcomesClinical practiceImputationModel specificationMissingnessData methodsModified dataTrials
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